Close the gap in treatment of spinal muscular atrophy

AS we observe Rare Disease Day at the end of this month, it is crucial to highlight the challenges faced by individuals living with spinal muscular atrophy (SMA) in this country.

SMA is a rare genetic condition that progressively weakens muscles, significantly impacting mobility, breathing, and overall quality of life. Despite advancements in medical science, many Malaysian families continue to face significant hurdles in managing the condition, including delayed diagnoses, limited access to treatment, and the heavy financial burden.