Support for rare disease sufferers

SPINAL muscular atrophy (SMA) is a rare disease that used to lead to no other outcome but premature death. And before that death, children would suffer dreadful deterioration of the ability to move, eat and breathe. In a majority of cases, that traumatic end used to come before two years of age; SMA was known as a major cause of the death of babies under that age.

However, with advancements in science and medicine, the outcome for SMA patients has dramatically changed. Today, there are two drug therapies that can stop this disease and save lives. Lives that carry a huge amount of potential if one were to look at the achievements of those with SMA who have survived to excel in the arts, entrepreneurship, academia and many other fields.