IN mid-2018, a diverse group of stakeholders urged the government to provide life-saving drug therapy for Malaysians devastated by a genetic disorder known as spinal muscular atrophy (SMA).
Close to 50 other countries provide a drug therapy using nusinersen (marketed as Spinraza), and many will soon also provide the gene medication onasemnogene abeparvovec (marketed as Zolgensma). We can expect a third drug therapy called Risdiplam to be filed for approval by the end of this year.
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